World Orphan Drug Congress USA

The World Orphan Drug Congress brings together leading pharmaceutical and biotech companies, government and regulatory authorities, patient advocacy groups, payers, investors and solution providers. The conference is a place to meet and brainstorm ways to advance orphan drug development and improve access to life-saving therapies.

Please come and visit us at Booth 507 in the exhibit hall, we would love to see you there. 

Parexel Presentations:

Keynote Panel

Advancing cell and gene therapies for rare diseases: What challenges face developers in pre-commercialization and how can all stakeholders work to get therapies to rare patients faster?

Izaskun Elorza, Senior Medical Director – Panel Moderator

09.45- July 12th

Speaking Session

Experience-based solutions for challenges on cell and gene clinical trials

Izaskun Elorza, Senior Medical Director

11.35 – July 12th

Roundtable

Patient Accessibility Challenges: Discussing real-world challenges identified from clinical trials and how patient accessibility issues can hinder product launch

Pam Rattananont, Director, Customer Strategy

2.00 – July 12th