Event Event

World Orphan Drug Congress US

April 23 - April 25, 2024

Boston, MA

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The World Orphan Drug Congress brings together leading pharmaceutical and biotech companies, government and regulatory authorities, patient advocacy groups, payers, investors and solution providers. The conference is a place to meet and brainstorm ways to advance orphan drug development and improve access to life-saving therapies. We look forward to seeing you there!

Hear from Parexel

Rachel Smith

Executive Director, Rare Disease, Center of Excellence

Moderator | Wednesday, April 24th from 10:05 – 10:45 am ​

Challenge and opportunity with the current regulatory and legislative landscape in the US​

Renata Gallagher, M.D., Ph.D.

Medical Director

Speaker | Wednesday, April 24th from 11:45 am – 12:05 pm ​

An honest discussion: the challenges of genotype interpretation and phenotype variation in rare disease ​

Kim MacDonnell

Associate Director, Rare Disease, Center of Excellence

Speaker | Wednesday, April 24th from 2:15 – 2:55 pm ​

Benefit or a threat? Beware the AI generated patient. ​

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