How real-world data is powering rare disease research Part 2. RWD advances in Europe
As real-world data (RWD) transforms the drug development landscape, its power to advance research is becoming tangible in the most challenging therapeutic arena—rare diseases. In this series, Parexel experts discuss current initiatives in North America, Europe and China that are accelerating the use of RWD in rare disease research.
Related Insights
Whitepaper
How real-world data is powering rare disease research Part 3. RWD advances in China
Apr 18, 2025
Blog
Studying rare cancer patient populations using integrated genomic and real-world data
Aug 30, 2023
Whitepaper
How real-world data is powering rare disease research Part 1. RWD advances in North America
Apr 18, 2025
Playbook
Insights from the 2022 R&D Innovation Survey
Feb 17, 2023
Blog
A hybrid model supports globally diverse site participation for a retrospective cancer study
Jul 24, 2023
Blog
Celebrating 40 Years of Rare Disease Progress: WODC Highlights
Jun 6, 2023
Webinar
Assessing appropriate use of ECAs in clinical trials
May 28, 2023
Webinar
Adaptive strategies for more efficient, data-rich and patient-friendly trials
May 28, 2023
Report
New Medicines, Novel Insights: Advancing rare disease drug development
May 22, 2023
Video
The science and practice of ethnobridging
May 17, 2023
Blog
Incorporating the patient voice in clinical research: Validation of COAs for a rare disease NDA
Nov 17, 2025
Playbook
Are you using real-world evidence?
Feb 1, 2023
Related Insights
Whitepaper
How real-world data is powering rare disease research Part 3. RWD advances in China
Apr 18, 2025
Blog
Studying rare cancer patient populations using integrated genomic and real-world data
Aug 30, 2023
Whitepaper
How real-world data is powering rare disease research Part 1. RWD advances in North America
Apr 18, 2025
Playbook
Insights from the 2022 R&D Innovation Survey
Feb 17, 2023
Blog
A hybrid model supports globally diverse site participation for a retrospective cancer study
Jul 24, 2023
Blog
Celebrating 40 Years of Rare Disease Progress: WODC Highlights
Jun 6, 2023
Webinar
Assessing appropriate use of ECAs in clinical trials
May 28, 2023
Webinar
Adaptive strategies for more efficient, data-rich and patient-friendly trials
May 28, 2023
Report
New Medicines, Novel Insights: Advancing rare disease drug development
May 22, 2023
Video
The science and practice of ethnobridging
May 17, 2023
Blog
Incorporating the patient voice in clinical research: Validation of COAs for a rare disease NDA
Nov 17, 2025
Playbook
Are you using real-world evidence?
Feb 1, 2023