Gene Therapy for Rare Disorders

Gene Therapy for Rare Disorders is dedicated to overcoming the unique drug development challenges encountered in transforming gene therapy concepts into reality for rare disease patients in need.

As the gene therapy field strives to strike the balance between clinical efficacy and product safety in the context of mounting regulatory scrutiny, Gene Therapy for Rare Disorders 2022 will provide in-depth insights from experts who know how to drive clinical progress, optimize manufacturing, and demonstrate the value of gene therapy products to regulators, payers, and patients.

Parexel Presentation:
March 9, 11:30am
Preclinical Regulatory Challenges for Genome Editing Products
Lu Wing, Vice President, Technical

You will also find us in the Exhibit Hall.